The WORLDSymposium 2021 Virtual Platform: Click HERE for information.


WORLDSymposium 2021 will feature over 330 scientific abstracts presented at five separate poster sessions. These sessions are an excellent opportunity to discuss concepts, share knowledge, and exchange ideas directly with the abstract authors and other WORLDSymposium participants. Click here for more information and to download the list.


The Full Program for WORLDSymposium 2021 is now available. Five full days of new discoveries, cutting-edge research, and updates from ongoing studies will be presented by scientists and clinicians from around the globe, including ground-breaking presentations from industry leaders in the Contemporary Forum on Thursday, and the new Late-Breaking Science presentations on Friday.

Peter Marks, MD, PhD, to Deliver Keynote Address on Thursday, February 11, 2021

Peter Marks WORLDSymposium 2021 Keynote SpeakerThe WORLDSymposium Planning Committee is excited to announce Peter Marks, MD, PhD, will provide the Keynote Address on Thursday, February 11, 2021 at the 17th Annual WORLDSymposium Scientific Meeting.

Dr. Marks is the director of the Center for Biologics Evaluation and Research (CBER) at the U.S. Food and Drug Administration (FDA). The center is responsible for assuring the safety and effectiveness of biological products, including vaccines, allergenic products, blood and blood products, and cellular, tissue, and gene therapies.

Dr. Marks presented a Keynote Address at WORLDSymposium in February 2020. Almost exactly one year later, a very different world and a very different experience presents itself to all attendees.Dr. Marks will be presenting “Trailblazing a Regulatory Framework for Individualized Therapies” as the Keynote Address on Thursday, February 11, 2021 at 8:45 AM Eastern Standard Time (EST). His presentation will provide a distinct and highly informed perspective on individualized therapeutics.

Click here to read more.

Michael T. Osterholm, Phd, MPH, to Deliver Keynote Address on Wednesday, February 10, 2021

Michael T. Osterholm, Phd, MPH The WORLDSymposium Planning Committee is excited to announce Michael T. Osterholm, PhD, MPH, will provide the Keynote Address on Wednesday, February 10, 2021 at the 17th Annual WORLDSymposium Virtual Scientific Meeting.

Dr. Osterholm is Regents Professor, McKnight Presidential Endowed Chair in Public Health, the director of the Center for Infectious Disease Research and Policy (CIDRAP), Distinguished Teaching Professor in the Division of Environmental Health Sciences, School of Public Health, a professor in the Technological Leadership Institute, College of Science and Engineering, and an adjunct professor in the Medical School, all at the University of Minnesota. From June 2018 through May 2019, he served as a Science Envoy for Health Security on behalf of the US Department of State. He is also on the Board of Regents at Luther College in Decorah, Iowa.

The Deadliest Enemy by Michael T. Osterholm, Phd, MPHHe is the author of the 2017 book, Deadliest Enemy: Our War Against Killer Germs, in which he not only details the most pressing infectious disease threats of our day but lays out a nine-point strategy on how to address them, with preventing a global flu pandemic at the top of the list.

Dr. Osterholm will be presenting “The COVID Pandemic: The Evolving Reality” as the Keynote Address on Wednesday, February 10, 2021 at 9:00 AM EST.  Make sure this session is on your calendar to hear Dr. Osterholm’s important message.

Click here to read more.


Each year, trainees and recent doctoral graduates are encouraged to apply for the WORLDSymposium Young Investigator Award. The Young Investigator Award provides a partial scholarship to attend WORLDSymposium 2021. Award recipients will be recognized at the 2021 Scientific Meeting on Friday, February 12, 2021 at 8:45 AM Eastern Standard Time (EST).

Click here for the full announcement.

WORLDSymposium 2021 will be Virtual-only

WORLDSymposium, in consideration of the ongoing uncertainty surrounding the COVID-19 pandemic, announces that it will transition the 2021 Annual Scientific Meeting, scheduled for February 8-12, 2021, to an entirely virtual meeting. The health and safety of attendees, faculty, sponsors and staff remains the primary concern of the WORLDSymposium.

The decision to go virtual will allow WORLDSymposium to provide the best possible meeting experience while guaranteeing everyone’s well-being. WORLDSymposium will present this year’s Annual Meeting with a fresh, new approach to the informative and inspiring event so many professionals and researchers look forward to each year. The virtual platform will allow attendees from around the globe to access the meeting’s program of activities and content, and network with other attendees and companies online. There is also the expectation that many of the innovations incorporated into this year’s meeting will be added to future in-person meetings.

If you have already registered for the in-person meeting, thank you for your interest and support. You will be contacted shortly in order to update your registration and to provide you any necessary refunds.

WORLDSymposium Announces Ellen Sidransky, MD as Recipient of 2021 Roscoe O. Brady Award for Innovation and Accomplishment

Ellen Sidransky, MDEach year, WORLDSymposium recognizes one individual for innovation and accomplishment in the field of lysosomal disease research and therapy. After reviewing numerous nominations, and considering many amazing individuals, the WORLDSymposium 2021 Awards Committee has selected Ellen Sidransky, MD, Chief, Section on Molecular Neurogenetics, Medical Genetics Branch, National Human Genome Research Institute, as the recipient of the 2021 Roscoe O. Brady Award for Innovation and Accomplishment.

Click here to read more.

Terri L. Klein to receive the WORLDSymposium 2021 Patient Advocate Leader (PAL) Award

Terri Klein, NPGC - Patient Advocate Leader Award Recipient 2021 Congratulations to Terri L. Klein, NPGC, the recipient of the WORLDSymposium™ 2021 Patient Advocate Leader (PAL) Award. Terri is the President and CEO at the National MPS Society, USA, is the co-Chair of the International MPS Network (IMPSN) and and the Council of Patient Advocates (COPA), representing the NIH-funded Lysosomal Disease Network (LDN) consortium of the NIH Rare Disease Clinical Research Network, and is a founding member of the Mucolipidosis Research Collaborative Network. Recently formed in 2019, this novel group of scientists, researchers, clinicians, and patient advocates are working in tandem to discover the scientific answers to provide therapies for ML II/III. She is a wife and mother of four, including Jennifer (28), her youngest that suffers from ML III.

Click here to read more.

WORLDSymposium Online 1-hour CME Session: Cardiovascular Implications in Fabry Disease Now Available

WORLDSymposium has released a free one-hour online CME session “Cardiovascular Implications in Fabry Disease: A Multidisciplinary Approach”, available to all health care practitioners. The course is available at CME University and at myCME.

There is a required pre-test and post-test in order to obtain the credit.

If you are already registered with CME University or myCME, you may use your user name and password to login and complete the activity. If you are a new user, you will be prompted to set up a login so you can save your progress and credit history.

Claiming Educational Credits for the 2021 WORLDSymposium Meeting

Information on how to claim education credits is given only to registered attendees and is available in the 2021 virtual platform, WORLDSymposium mobile app or by contacting us.

Preliminary Schedule at A Glance

All times are US Eastern Standard Time (EST) Zone and schedule is subject to change

Day Sunday
Feb. 7, 2021
Feb. 8, 2021
Feb. 9, 2021
Feb. 10, 2021
Feb. 11, 2021
Feb. 12, 2021
Morning Emerging Trends 2021 (10:00 AM-2:00 PM) Basic Science: Disease Mechanisms, Pathology, and Biomarkers Translational Research Clinical Trials for Registration1 Contemporary Forum: Industry Abstracts from All Categories (Non-CME) Late-breaking Abstracts
Lunch Satellite Symposia Satellite Symposia Satellite Symposia Satellite Symposia Satellite Symposia
Afternoon Basic Science: Disease Mechanisms, Pathology, and Biomarkers Translational Research Clinical Trials for Registration2 Contemporary Forum: Industry Abstracts from All Categories (Non-CME) Late-breaking Abstracts
Poster Session I Poster Session II Poster Session III Poster Session IV Poster Session V
Evening Satellite Symposia Satellite Symposia Satellite Symposia Networking Reception (3:30-4:30 PM)
1 Abstracts in the Clinical Trials for Registration category must have an FDA Investigational New Drug (IND) application (Phase I-III clinical trial), an EMA Investigational Medicinal Product Dossier (IMPD), or equivalent.
2 The Clinical Outcomes category includes licensed therapies (Phase IV) and non-interventional studies.

We’re Organizing Research on Lysosomal Diseases

Dates to Remember

August 1, 2020
Abstract submission website open.

September 1, 2020
Registration for the conference opens. Distribution of exhibitor prospectus and support opportunities to all prior supporting companies, and also available by request.

October 1, 2020
Deadline for submission of full-length manuscripts for peer-review in the “Lysosomes” issue of Molecular Genetics & Metabolism, February, 2021. Click here to access the Guide for Authors or to Submit Your Paper.

October 1, 2020
Deadline for abstract submission to WORLDSymposium 2021.

November 1 – December 1,  2020
Late breaking abstract submission open.

November 15, 2020
Notification of abstract acceptance for poster or platform presentation at WORLDSymposium 2021.

About WORLDSymposium

The goal of WORLDSymposium is to provide an interdisciplinary forum to explore and discuss specific areas of interest, research and clinical applicability related to lysosomal diseases. Each year, WORLDSymposium hosts a scientific meeting presenting the latest information from basic science, translational research, and clinical trials for lysosomal diseases. This symposium is designed to help researchers and clinicians to better manage and understand diagnostic options for patients with lysosomal diseases, identify areas requiring additional basic and clinical research, public policy and regulatory attention, and identify the latest findings in the natural history of lysosomal diseases.

Sign up for Updates

Sign up for Updates

Click here to sign up for updates about the 17th Annual WORLDSymposium.

This symposium is designed for basic, translational and clinical researchers, patient advocacy groups, clinicians, and all others who are interested in learning more about the latest discoveries related to lysosomal diseases and the clinical investigation of these advances.