This new session: The Patient Voice: Is Anyone Listening? explored measures that industry and other researchers have taken to better understand what is most important to patients in terms of clinical trial endpoints, unmet needs, and goals of therapies. More details.
In 2024, WORLDSymposium presented the first “Catalyst” award to Zachary Thomas on Sunday, February 4, 2024. More details.
19 Satellite symposia were held from Monday, February 5, 2024 to Thursday, February 8, 2024 Click here for the full schedule.
After the presentation of the Innovation Award, the formal scientific sessions of WORLDSymposium 2024 officially begins with presentations on laboratory research for lysosomal disease. Presentations during the Basic Science sessions are designed to improve our understanding or prediction of the phenomena involved in lysosomal pathology at a molecular, cellular, and animal model level in order to forwardly think about diagnosis and treatment of lysosomal conditions. View full program.
WORLDSymposium 2024 Roscoe O. Brady Award was received by Elsa Shapiro, PhD for Innovation and Accomplishment on Monday, February 5, 2024, followed by a scientific presentation by Dr. Shapiro. More details.
WORLDSymposium 2024 attracted over 35 Exhibitors offering a highly interactive forum for discussion of lysosomal diseases with international researchers and health care practitioners. More details.
In 2024, over 450 scientific abstracts were presented at four separate poster sessions beginning on Monday, February 5, 2024, and remained open throughout the rest of the conference. More details.
3 Industry Expert Theaters were held from Tuesday, February 6, 2024 to Thursday, February 8, 2024. Click here for details.
The 2nd Annual Speed Mentoring Event featured 36 Mentors. 56 Individuals took advantage of this once-in-a-lifetime opportunity to meet with a wide variety of leaders and icons from the lysosomal and rare disease space.
WORLDSymposium was pleased to announce the recipients of the 2024 Young Investigator Awards on Tuesday, February 6, 2024. More details.
WORLDSymposium 2024 Patient Advocate Leader (PAL) Award was received by lan Finglas on Tuesday, February 6, 2024. Alan and his wife Michelle founded MSD Action Foundation & SavingDylan.com More details.
The 2024 session discussed current approaches for treating the central nervous system in lysosomal diseases. Presentations included an overview of current and future approaches for treating the central nervous system, and address challenges in identifying and implementing meaningful outcome measures for evaluating efficacy of central nervous system therapies. More details.
Dr. Marks’ Keynote Address: Accelerating the Pace of Progress in Gene Therapy, was on Wednesday, February 7, 2024 at 7:30 AM PST, at the 20th Annual WORLDSymposium in San Diego, California Read speaker bio.
The WORLDSymposium New Treatment Award for 2024 was presented to Amicus Therapeutics for ipaglucosidase alfa (Pombiliti®) and Chiesi Global Rare Diseases for pegunigalsidase alfa-iwxj (Elfabrio®) and for velmanase alfa-tycv (Lamzede®) More details.