Peter Marks to Deliver Keynote Address on Thursday, February 13, 2020

Peter Marks WORLDSymposium 2020 Keynote SpeakerThe WORLDSymposium Planning Committee is excited to announce Peter Marks, MD, PhD, as Keynote Speaker on Thursday, February 13, 2020 at the 16th Annual WORLDSymposium Scientific Meeting in Orlando, Florida, USA.

Dr. Marks is the director of the Center for Biologics Evaluation and Research (CBER) at the U.S. Food and Drug Administration (FDA). The center is responsible for assuring the safety and effectiveness of biological products, including vaccines, allergenic products, blood and blood products, and cellular, tissue, and gene therapies.

Dr. Marks will be presenting “The Shift from Personalized to Individualized Therapies” as the Keynote Address on Thursday, February 13, 2020 at 7:30 AM. Plan to arrive early on Thursday, as seating is expected to fill quickly for his important messages.

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WORLDSymposium Announces John F. Crowley as Recipient of 2020 Roscoe O. Brady Award for Innovation and Accomplishment

John F. Crowley, Amicus TherapeuticsEach year, WORLDSymposium requests nominations from the lysosomal disease community, and then recognizes one individual for innovation and accomplishment in the field of lysosomal disease research and therapy. After reviewing numerous nominations, and considering many amazing individuals, the WORLDSymposium 2020 Planning Committee selected nominee John F. Crowley to receive the 2020 Roscoe O. Brady Award for Innovation and Accomplishment.

The 2020 Roscoe O. Brady Award for Innovation and Accomplishment will be presented to John F. Crowley, Chairman of the Board, Chief Executive Officer, Amicus Therapeutics, Inc. on Tuesday, February 11, 2020 at 7:30 AM.

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WORLDSymposium Announces Cara O’Neill, MD as Recipient of the 2020 Patient Advocate Leader (PAL) Award

Cara O’Neill, MD - Patient Advocate Leader Award Recipient 2020Each year, WORLDSymposium recognizes one individual for patient advocacy leadership in the field of lysosomal disease. The 2020 Patient Advocate Leader (PAL) award will be presented to Cara O’Neill, MD, founder and Chief Science Officer at Cure Sanfilippo Foundation on Wednesday, February 12, 2020 at 7:30 AM.

Dr. ONeill and her husband founded Cure Sanfilippo Foundation after receiving her daughter’s diagnosis in 2013, guided by the mission to support the creation of treatments and an eventual cure for the disease. Since then, they have spread awareness around the globe about Sanfilippo syndrome via talk shows, news media, online platforms, and international newspapers.

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Call for Abstracts: WORLDSymposium™ 2020 Online Abstract Submission Now Closed

The deadline for submitting an abstract to WORLDSymposium was October 1, 2019 for review by the Program Committee. Abstracts must be submitted with the intention that they will be presented if selected. First authors are expected to attend the meeting and make the presentation. Authors should not submit abstracts if they do not plan to attend the meeting. The first author of the submitted abstract will be notified of acceptance for platform or poster presentation by November 15, 2019.

The WORLDSymposium late-breaking abstract submission site will be open from November 1 – December 1, 2019. Click here for more information. about late-breaking abstract submissions.


Monday, February 10, 2020: Opening Reception and Poster Session I

This year, Monday evening will include an Opening Reception and the first of three Poster Sessions in the Exhibit Hall. Plan to arrive early for this special event.


Claiming Educational Credits for the 2019 WORLDSymposium Meeting

Information on how to claim education credits is given only to registered attendees and is available in the 2019 WORLDSymposium mobile app or by contacting us.


Preliminary Schedule at A Glance

Day Monday
Feb. 10, 2020
Tuesday
Feb. 11, 2020
Wednesday
Feb. 12, 2020
Thursday
Feb. 13, 2020
6:15-7:15 AM Satellite Symposia Satellite Symposia Satellite Symposia
Morning Emerging Trends 2020 (8:00-11:30 AM) Basic Science: Disease Mechanisms, Pathology, and Biomarkers Translational Gene Therapy Translational Studies Clinical Trial Outcomes2
Lunch Satellite Symposia Satellite Symposia Satellite Symposia Satellite Symposia
Afternoon Basic Science: Disease Mechanisms, Pathology, and Biomarkers Translational Research (including Newborn Screening) Clinical Trials for Registration1 NEW Contemporary Forum: Industry Abstracts from All Categories (Non-CME)
4:30-6:30 PM Opening Reception & Poster Reception I Poster Reception II Poster Reception III Networking Reception (4:30-5:30 PM)
6:30-8:30 PM Satellite Symposia Satellite Symposia Satellite Symposia Lysosomal Disease Network (LDN) COPA and Council of Research Experts (CORE) (5:00 – 7:00 PM)
1 Abstracts in the Clinical Trials for Registration category must have an FDA Investigational New Drug (IND) application (Phase I-III clinical trial), an EMA Investigational Medicinal Product Dossier (IMPD), or equivalent.
2 The Clinical Outcomes category includes licensed therapies (Phase IV) and non-interventional studies.

We’re Organizing Research on Lysosomal Diseases

Dates to Remember

July 25, 2019
Abstract submission website open.

August 1, 2019
Online registration and hotel reservations open.

August 9, 2019
Exhibitor prospectus available by request.

September 1, 2019
Deadline for submission of full-length manuscripts for peer-review in the “Lysosomes” issue of Molecular Genetics & Metabolism, February, 2020. Click here to access the Guide for Authors or to Submit Your Paper.

October 1, 2019
Deadline for abstract submission to WORLDSymposium 2020.

November 1 – December 1,  2019
Late breaking abstract submission open.

November 5, 2019
Notification of abstract acceptance for poster or platform presentation at WORLDSymposium 2020.

About WORLDSymposium

The goal of WORLDSymposium is to provide an interdisciplinary forum to explore and discuss specific areas of interest, research and clinical applicability related to lysosomal diseases. Each year, WORLDSymposium hosts a scientific meeting presenting the latest information from basic science, translational research, and clinical trials for lysosomal diseases. This symposium is designed to help researchers and clinicians to better manage and understand diagnostic options for patients with lysosomal diseases, identify areas requiring additional basic and clinical research, public policy and regulatory attention, and identify the latest findings in the natural history of lysosomal diseases.

Sign up for Updates

Sign up for Updates

Click here to sign up for updates about the 16th Annual WORLDSymposium.

This symposium is designed for basic, translational and clinical researchers, patient advocacy groups, clinicians, and all others who are interested in learning more about the latest discoveries related to lysosomal diseases and the clinical investigation of these advances.