
NEW THIS YEAR
Be the Catalyst Event
Tuesday, February 21, 2023
6:00 PM to 7:30 PM
“Be the Catalyst” is an exciting new event, open to all WORLDSymposium participants. This new event will provide a great opportunity to reconnect with colleagues, make new connections, establish new relationships, welcome new attendees, and celebrate the achievements of past and present WORLDSymposium Award Recipients.
2023 NEW TREATMENT AWARD ANNOUNCED
WORLDSymposium is pleased to announce the recipients of the 2023 New Treatment Award. Congratulations! Read full announcement here.
2023 YOUNG INVESTIGATOR AWARDS ANNOUNCED
WORLDSymposium is pleased to announce the recipients of the 2023 Young Investigator Award. Congratulations to this year’s recipients! Read full announcement here.
PETER MARKS, MD, PhD RETURNS AS KEYNOTE SPEAKER ON FRIDAY, FEBRUARY 24, 2023

WORLDSymposium is excited to announce the return of Peter Marks, MD, PhD, director of the Center for Biologics Evaluation and Research (CBER) at the Food and Drug Administration, as the 2023 Keynote Speaker. Dr. Marks gave presentations to the WORLDSymposium audience in 2020 and 2021, providing important updates on the FDA’s role in rare disease research, and he will present the 2023 Keynote Address on Friday, February 24, 2023.
Dr. Marks’ Keynote Address: Taking Gene Therapy to the Next Level, on Friday, February 24, 2023 at 7:30 AM EST, at the 19th Annual WORLDSymposium in Orlando, Florida. Read full announcement here.
WORLDSymposium ANNOUNCES CHRISTINE WAGGONER AS RECIPIENT OF 2023 PATIENT ADVOCATE LEADER AWARD

Congratulations to Christine Waggoner, the recipient of the WORLDSymposium 2023 Patient Advocate Leader (PAL) Award. After reviewing numerous nominations, and considering many amazing individuals, the WORLDSymposium 2023 Awards Committee has selected Christine as the recipient of the 2023 PAL Award. Christine founded the Cure GM1 Foundation in April 2015 in honor of her daughter Iris and all those affected by GM1 gangliosidosis. Christine’s work at Cure GM1 has involved a broad range, including animal models, biomarkers, gene therapy, enzyme replacement therapy, patient registries, patient reported outcomes, newborn screening and the first-ever GM1 caregiver preferences study. Read full announcement here.
WORLDSymposium ANNOUNCES WILLIAM A. GAHL, MD, PHD, AS RECIPIENT OF 2023 ROSCOE O. BRADY AWARD

Each year, WORLDSymposium recognizes one individual for innovation and accomplishment in the field of lysosomal disease research and therapy. After reviewing numerous nominations, and considering many amazing individuals, the WORLDSymposium 2023 Awards Committee has selected William A. Gahl, MD, PhD, as the recipient of the 2023 Roscoe O. Brady Award. Dr. Gahl is the Director of the Undiagnosed Diseases Program, a Senior Investigator in the Medical Genetics Branch and the Head of the Human Biochemical Genetics Section of the National Human Genome Research Institute (NHGRI). Read full announcement here.
About WORLDSymposium
WORLDSymposium™ is an annual research conference dedicated to lysosomal diseases.
WORLD is an acronym that stands for We’re Organizing Research on Lysosomal Diseases.
The goal of WORLDSymposium is to provide an interdisciplinary forum to explore and discuss specific areas of interest, research and clinical applicability related to lysosomal diseases. Each year, WORLDSymposium hosts a scientific meeting presenting the latest information from basic science, translational research, and clinical trials for lysosomal diseases. This symposium is designed to help researchers and clinicians to better manage and understand diagnostic options for patients with lysosomal diseases, identify areas requiring additional basic and clinical research, public policy and regulatory attention, and identify the latest findings in the natural history of lysosomal diseases.

WORLDSymposium 2023 REGISTRATION NOW OPEN
Plan to attend the 19th Annual WORLDSymposium Research Meeting February 22 – 26, 2023 at the Hilton Orlando in Orlando, FL, USA.
This symposium is designed for basic, translational and clinical researchers, patient advocacy groups, clinicians, and all others who are interested in learning more about the latest discoveries related to lysosomal diseases and the clinical investigation of these advances.
Plans are in place for a LIVE in-person gathering in Orlando at the Hilton Orlando Hotel. In addition, plans are underway to make the program available ON DEMAND after the conference ends to allow for registration for those who are unable to attend in person.
CLAIMING EDUCATIONAL CREDITS FOR THE 2022 WORLDSymposium MEETING
Information on how to claim education credits is given only to registered attendees and is available in the 2022 WORLDSymposium mobile app.
Preliminary Schedule at a Glance
Schedule is subject to change
Download: WORLDSymposium 2023 Schedule at a Glance
Day | Tuesday Feb. 21, 2023 | Wednesday Feb. 22, 2023 | Thursday Feb. 23, 2023 | Friday Feb. 24, 2023 | Saturday Feb. 25, 2023 | Sunday Feb. 26, 2023 |
---|---|---|---|---|---|---|
Satellite Symposia | Satellite Symposia | Satellite Symposia | Satellite Symposia | |||
Morning | Roscoe. O. Brady Award Basic Science | Patient Advocate Leader & Young Investigator Awards Translational Research | Keynote Address Clinical Applications | New Treatment Award Contemporary Forum (Non-CME) | Late-breaking Science | |
Midday | Satellite Symposia | Satellite Symposia | Satellite Symposia | Satellite Symposia | 11:15 AM Adjourn | |
Afternoon | Robert J. Gorlin Symposium | Basic Science | Translational Research | Clinical Applications | Contemporary Forum (Non-CME) | |
Emerging Trends | Poster Session I & II | Poster Session III & IV | Poster Session V & VI | Poster Session VII & VIII | ||
Evening | Be the Catalyst Event | Speed Mentoring Event | Satellite Symposia | Satellite Symposia |
Plan on attending the
19th Annual WORLDSymposium
February 21, 2023: Robert J. Gorlin Symposium and Emerging Trends
February 22-26, 2023: Research Meeting
Hilton Orlando, Orlando, FL, USA
Scientific Meeting Location & Accommodations
Hilton Orlando
6001 Destination Parkway
Orlando Florida, USA, 32819
Phone: +1-407-313-4300
Website: hilton.com
Website: thehiltonorlando.com
Letters of Invitation
Your meeting registration confirmation will include a link to generate a customized letter of invitation, which can be used when applying for a visa.

Dates to Remember
July 1, 2022
Abstract submission website open.
August 1, 2022
Registration for the conference opens. Distribution of exhibitor prospectus and support opportunities to all prior supporting companies, and also available by request.
October 1, 2022
Deadline for abstract submission to WORLDSymposium 2023.
October 1, 2022
Deadline for submission of full-length manuscripts for peer-review in the “Lysosomes” issue of Molecular Genetics & Metabolism, February, 2023. Click here to access the Guide for Authors or to Submit Your Paper.
November 1 – December 1, 2022
Late breaking abstract submission open.
November 15, 2022
Notification of abstract acceptance for poster or platform presentation at WORLDSymposium 2023.