TIPPI MACKENZIE, MD ANNOUNCED AS KEYNOTE SPEAKER ON WEDNESDAY, FEBRUARY 9, 2022

Tippi MacKenzie is a Professor of Surgery at the University of California, San Francisco and the Director of the Eli and Edythe Broad Institute for Regeneration Medicine. She is a pediatric and fetal surgeon who is focused on developing better ways to diagnose and treat genetic diseases before birth. She runs a translational research lab examining fetal immunology and maternal-fetal tolerance, with the ultimate goal of inventing new fetal therapies for patients with genetic diseases or pregnancy complications. She has moved two fetal molecular therapies from the lab to the clinic as phase 1 clinical trials after obtaining FDA approval: in utero hematopoietic stem cell transplantation to treat fetuses with alpha thalassemia and in utero enzyme replacement therapy in fetuses with lysosomal storage disorders.

Plan to attend Dr. MacKenzie’s Keynote Address at 7:30 AM PST on Wednesday, February 9, 2022, at the 18th Annual WORLDSymposium in San Diego, California.

Click here to read more.


Sue Kahn to receive the WORLDSymposium™ 2022 Patient Advocate Leader (PAL) Award

Sue Kahn NTSAD PAL AwardCongratulations to Sue Kahn, the recipient of the WORLDSymposium 2022 Patient Advocate Leader (PAL) Award. Sue is a leader known for her business acumen and ability to build relationships, collaborate, and drive research at one of the oldest and most respected patient advocacy groups in the rare disease community. For 14 years, she has served as the Executive Director of the National Tay-Sachs & Allied Diseases Association (NTSAD) that supports families affected by Tay-Sachs, Canavan, GM1, and Sandhoff.

The 2022 Patient Advocate Leader Award will be presented at 7:30 AM PST on Tuesday, February 8, 2022, at the 18th annual WORLDSymposiumin San Diego, California.

Click here to read more.


WORLDSymposium™ 2022 REGISTRATION NOW OPEN

Plan to attend the 18th Annual WORLDSymposium February February 7 – 11, 2022 at the Manchester Grand Hyatt in San Diego, CA, USA.

This symposium is designed for basic, translational and clinical researchers, patient advocacy groups, clinicians, and all others who are interested in learning more about the latest discoveries related to lysosomal diseases and the clinical investigation of these advances.

Click here to register.


CALL FOR ABSTRACTS: WORLDSymposium 2022 ONLINE ABSTRACT SUBMISSION NOW OPEN

Abstract Submission Highlights: Individuals are encouraged to submit their research on RNA therapies, gene editing, lentiviral ex vivo gene therapies, newborn screening, COVID research related to lysosomal diseases, and any other research applicable to lysosomal disorders during the Open Call for Abstracts from July 1 to October 1, 2021.

The deadline for submitting an abstract to WORLDSymposium is October 1, 2021 for review by the Program Committee. Abstracts must be submitted with the intention that they will be presented if selected. First authors are expected to attend the meeting and make the presentation. Authors should not submit abstracts if they do not plan to attend the meeting. Click here for more information.


WORLDSymposium 2022 AWARD NOMINATIONS NOW CLOSED

Nominations for the Roscoe O. Brady Award for Innovation and Accomplishment and the Patient Advocate Leader Award opened July 1, 2021. Awards will be presented at WORLDSymposium 2022. Nominations Deadline was August 15, 2021.


CLAIMING EDUCATIONAL CREDITS FOR THE 2021 WORLDSymposium MEETING

Information on how to claim education credits is given only to registered attendees and is available in the 2021 WORLDSymposium mobile app or by contacting us.


WORLDSymposium 2021 VIRTUAL MEETING: ATTENDEE INFORMATION

The WORLDSymposium 2021 Virtual Platform: Click HERE for information.


Preliminary LIVE Schedule at A Glance

Schedule is subject to change

Day Sunday
Feb. 6, 2022
Monday
Feb. 7, 2022
Tuesday
Feb. 8, 2022
Wednesday
Feb. 9, 2022
Thursday
Feb. 10, 2022
Friday
Feb. 11, 2022
Morning Lysosomal Disease Network (LDN) Annual Meeting Basic Science: Disease Mechanisms, Pathology, and Biomarkers Translational Research Clinical Applications1 Contemporary Forum: Industry Abstracts from All Categories (Non-CME) Satellite Symposia
Late-breaking Abstracts
Poster Session V
Lunch Satellite Symposia Satellite Symposia Satellite Symposia Satellite Symposia 12:00 PM Adjourn
Afternoon Robert J. Gorlin Symposium Basic Science: Disease Mechanisms, Pathology, and Biomarkers Translational Research Clinical Applications1 Contemporary Forum: Industry Abstracts from All Categories (Non-CME)
Poster Session I Poster Session II Poster Session III Poster Session IV
Evening Satellite Symposia Satellite Symposia Satellite Symposia Satellite Symposia
1 Clinical Applications includes  Clinical Trials for Registration abstracts,  (which must have an FDA Investigational New Drug (IND) application (Phase I-III clinical trial), an EMA Investigational Medicinal Product Dossier (IMPD), or equivalent) and Clinical Outcomes abstracts including licensed therapies (Phase IV) and non-interventional studies.

We’re Organizing Research on Lysosomal Diseases

Dates to Remember

July 1, 2021
Abstract submission website open.

August 1, 2021
Registration for the conference opens. Distribution of exhibitor prospectus and support opportunities to all prior supporting companies, and also available by request.

October 1, 2021
Deadline for submission of full-length manuscripts for peer-review in the “Lysosomes” issue of Molecular Genetics & Metabolism, February, 2022. Click here to access the Guide for Authors or to Submit Your Paper.

October 1, 2021
Deadline for abstract submission to WORLDSymposium 2022.

November 1 – December 1,  2021
Late breaking abstract submission open.

November 15, 2021
Notification of abstract acceptance for poster or platform presentation at WORLDSymposium 2022.

About WORLDSymposium

The goal of WORLDSymposium is to provide an interdisciplinary forum to explore and discuss specific areas of interest, research and clinical applicability related to lysosomal diseases. Each year, WORLDSymposium hosts a scientific meeting presenting the latest information from basic science, translational research, and clinical trials for lysosomal diseases. This symposium is designed to help researchers and clinicians to better manage and understand diagnostic options for patients with lysosomal diseases, identify areas requiring additional basic and clinical research, public policy and regulatory attention, and identify the latest findings in the natural history of lysosomal diseases.

Sign up for Updates

Sign up for Updates

Click here to sign up for updates about the 18th Annual WORLDSymposium.

This symposium is designed for basic, translational and clinical researchers, patient advocacy groups, clinicians, and all others who are interested in learning more about the latest discoveries related to lysosomal diseases and the clinical investigation of these advances.