2023 Satellite Symposia Schedule

Satellite Symposia will be offered in the following times (subject to review and approval of content).

Wednesday, February 22, 2023, 6:15 AM – 7:15 AM
Exploring Next-generation Therapies to Mitigate Disease Progression in Pompe Disease
Supported by Amicus Therapeutics, Inc.

Wednesday, February 22, 2023, 6:15 AM – 7:15 AM
eDiagnosis: Innovations to Shorten the Rare Disease Diagnostic Journey
Supported by Sanofi

Wednesday, February 22, 2023, 11:45 AM – 12:45 PM
From Assay to Application.
Writing the roadmap for metachromatic leukodystrophy newborn screening

Supported by Orchard Therapeutics

Wednesday, February 22, 2023, 11:45 AM – 12:45 PM
First for Fabry Disease: 20-years of Clinical and Real-World Evidence
Supported by Sanofi

Thursday, February 23, 2023, 6:15 AM – 7:15 AM
A treatment option for non-CNS manifestations of ASMD: Patient and HCP perspectives on the transforming ASMD landscape
Supported by Sanofi

Thursday, February 23, 2023, 6:15 AM – 7:15 AM
Manifestations of Gaucher Disease: Rare or Under-recognized?
CE Satellite Symposium
Accredited provider: CME Outfitters
Supported by an independent educational grant from Takeda Pharmaceutical Company Limited.

Thursday, February 23, 2023, 11:45 AM – 12:45 PM
The Next Step Forward: Real World Experience in Patients with Late-Onset Pompe Disease
Supported by Sanofi

Thursday, February 23, 2023, 11:45 AM – 12:45 PM
Defining Patient-focused Outcomes in Fabry Disease
Supported by Amicus Therapeutics, Inc.

Thursday, February 23, 2023, 5:15 PM – 6:15 PM
Understanding Phenotypic Variability in Lysosomal Diseases – Gaining a Foothold in Precision Medicine
Takeda Pharmaceutical Company Limited

Thursday, February 23, 2023, 5:15 PM – 6:15 PM
Fabry Disease is a Pediatric Disease
Supported by Sanofi

Friday, February 24, 2023, 6:15 AM – 7:15 AM
Following a path to multisystemic efficacy in Fabry disease
Amicus Therapeutics, Inc.
This satellite is open only to registered attendees from outside the United States. International participants only.

Friday, February 24, 2023, 6:15 AM – 7:15 AM
Uncovering the neurologic impact of enzyme deficiencies along the glycosphingolipid pathway: A case-based discussion
Supported by Sanofi

Friday, February 24, 2023, 11:45 AM – 12:45 PM
Challenges in delivering ERT in lysosomal disorders: special considerations in LOPD
Supported by Amicus Therapeutics, Inc.

Friday, February 24, 2023, 11:45 AM – 12:45 PM
AAV Gene Therapy as a Potential Treatment Modality for Neuronopathic MPS II
Supported by REGENXBIO Inc.

Friday, February 24, 2023, 5:15 PM – 6:15 PM
One size does not fit all: Monitoring and management of anti-drug antibodies in lysosomal diseases with a focus on Fabry disease
Supported by Chiesi Global Rare Diseases

Friday, February 24, 2023, 5:15 PM – 6:15 PM
MPS IVA in adulthood: Recent findings from the largest global MPS IVA Registry Study
Supported by BioMarin Pharmaceutical Inc.

Saturday, February 25, 2023, 6:15 AM – 7:15 AM
Identifying, Monitoring, and Addressing Risk Factors Impacting Long-term Cardiac, Renal, and Neurological Disease Progression and Clinical Outcomes for Patients with Fabry Disease
CE Satellite Symposium
Accredited provider: Med Learning Group
Supported by an independent educational grant from Sanofi.

Saturday, February 25, 2023, 11:45 AM – 12:45 PM
The Rare Disease Ecosystem: A multi-stakeholder perspective on collaboration
Supported by Sanofi

Saturday, February 25, 2023, 11:45 AM – 12:45 PM
Pinpointing Alpha-Mannosidosis on the Map: Insights from the diagnostic odyssey of patients
Supported by Chiesi Global Rare Diseases

These Satellite Symposia are not part of the official WORLDSymposium™ program, and WORLDSymposium does not approve or endorse any commercial products or services discussed during the Satellite Symposia or offered for sale by any corporate supporter of the Satellite Symposia. These symposia may or may not offer CME credits; these sessions are not approved for CME through WORLDSymposium.

Eligibility: Registration for WORLDSymposium 2023 and an official name badge are required to attend satellite symposia.