WORLDSymposium 2017 Patient Advocate Leader (PAL) Award

WORLDSymposium 2017 Patient Advocate Leader (PAL) Award was received by Christine Lavery, MBE on Thursday, February 16, 2017. Christine Lavery founded the United Kingdom (UK) Society for Mucopolysaccharide Diseases (MPS Society) in 1982 following the death of her firstborn son, Simon, from Hunter disease. More details.

WORLDSymposium 2017 Roscoe O. Brady Award

WORLDSymposium 2017 Roscoe O. Brady Award was received by Konrad Sandhoff, PhD for Innovation and Accomplishment on Tuesday, February 14, 2017. Konrad Sandhoff completed his PhD in biochemistry in Munich. After early research in Munich, Israel and the USA, he became Professor of Biochemistry at the University of Bonn in 1979. More details.

WORLDSymposium 2017 Program

Following the presentation of the Award for Innovation and Accomplishment in lysosomal disease research, presentations in the morning and afternoon sessions will discuss innovations in technology and how they can be applied to early diagnosis for lysosomal conditions, progress in gene therapy, and exploitation of differences at the cellular level that may indicate early disease state. View full program.