WORLDSymposium 2017 Program

Following the presentation of the Award for Innovation and Accomplishment in lysosomal disease research, presentations in the morning and afternoon sessions will discuss innovations in technology and how they can be applied to early diagnosis for lysosomal conditions, progress in gene therapy, and exploitation of differences at the cellular level that may indicate early disease state. View full program.

WORLDSymposium 2017 Keynote Speakers

Dr. Elsa Shapiro’s Keynote Address: Understanding and Measuring Neurodegeneration in Childhood Onset Lysosomal Diseases, was on Wednesday, February 15, 2017 at 7:45 AM as well as Dr. Richard Moscicki’s Keynote Address: An FDA Perspective on Rare Disease Drug Development, was on Thursday, February 16, 2017, from 7:45-8:15 AM. Read speaker bios.

WORLDSymposium 2017 Patient Advocate Leader (PAL) Award

WORLDSymposium 2017 Patient Advocate Leader (PAL) Award was received by Christine Lavery, MBE on Thursday, February 16, 2017. Christine Lavery founded the United Kingdom (UK) Society for Mucopolysaccharide Diseases (MPS Society) in 1982 following the death of her firstborn son, Simon, from Hunter disease. More details.