WORLDSymposium 2020 Program

Following Emerging Trends in the morning and the Young Investigator Awards, presentations in the afternoon session discussed innovations in technology and how they can be applied to early diagnosis for lysosomal conditions, progress in gene therapy, and exploitation of differences at the cellular level that may indicate early disease state. View full program.

WORLDSymposium 2020 Roscoe O. Brady Award

WORLDSymposium 2020 Roscoe O. Brady Award was presented to John F. Crowley, MD on Tuesday, February 11, 2020 at 7:30 AM, followed by a scientific presentation by Dr. Crowley: The Moral Obligation to Ensure Access to Medicines for All Patients in Need. View details.

WORLDSymposium 2020 Patient Advocate Leader (PAL) Award

WORLDSymposium 2020 Patient Advocate Leader (PAL) Award was received by Cara O’Neill, MD on Wednesday, February 12, 2020. Cara O’Neill, MD, is the Chief Science Officer at Cure Sanfilippo Foundation, a pediatrician, and mother to a daughter with the rare disease Sanfilippo syndrome (MPS III). More details.

WORLDSymposium 2020 Keynote Speakers

Dr. Chester B. Whitley’s Keynote Address: Navigating Clinical Trials, was on Wednesday, February 12, 2020 as well as Dr. Peter Marks’ Keynote Address: The Shift from Personalized to Individualized Therapies, on Thursday, February 13, 2020 at 7:30 AM. Read speaker bios.