WORLDSymposium 2023 New Treatment Award

2023 New Treatment Award WORLDSymposium — Chester B. Whitley, Bill Sibold, Monica Kumar, Alaa Hamed, Shannon Resetich, Paul Hudson

The WORLDSymposium New Treatment Award for 2023 was presented to Sanofi for olipudase alfa-rpcp (Xenpozyme™) which provided clinical data meriting approval by the U.S. Food and Drug Administration (FDA) as the first disease-specific treatment of non-central nervous system (non-CNS) manifestations of acid sphingomyelinase deficiency (ASMD) in adult and pediatric patients. The New Treatment Award was presented on Saturday, February 25, 2023, at 7:45 AM EST, followed by a full day of Contemporary Forum abstract presentations.