WORLDSymposium 2026 Keynote Speaker
Dr. Michael H. Gelb’s Keynote Address: Biochemical Newborn Screening for All Treatable Lysosomal Diseases, was on Thursday, February 5, 2026, at 08:00 PST. Read speaker bio.
Dr. Michael H. Gelb’s Keynote Address: Biochemical Newborn Screening for All Treatable Lysosomal Diseases, was on Thursday, February 5, 2026, at 08:00 PST. Read speaker bio.
Dr. Peter Marks’ Keynote Address: Advancing the Frontier of Gene Therapy, was on Thursday, February 6, 2025 at 07:30 PST. Read speaker bio.
Dr. Peter Marks’ Keynote Address: Accelerating the Pace of Progress in Gene Therapy, was on Wednesday, February 7, 2024 at 7:30 AM PST. Read speaker bio.
Dr. Peter Marks’ Keynote Address: Taking Gene Therapy to the Next Level, was on Friday, February 24, 2023 at 7:30 AM EST. Read speaker bio.
Dr. Tippi MacKenzie’s Keynote Address: Prenatal enzyme replacement therapy for lysosomal disorders: Launching a phase I clinical trial, was on Wednesday, February 9, 2022, at 7:30 AM PST. Read speaker bio.
Dr. Michael T. Osterholm’s Keynote Address: The COVID Pandemic: The Evolving Reality, was on Wednesday, February 10, 2021 at 9:00 AM EST as well as Dr. Peter Marks’ Keynote Address: Trailblazing a Regulatory Framework for Individualized Therapies, on Thursday, February 11, 2021 at 8:45 AM Eastern Standard Time (EST). Read speaker bios.
Dr. Chester B. Whitley’s Keynote Address: Navigating Clinical Trials, was on Wednesday, February 12, 2020 as well as Dr. Peter Marks’ Keynote Address: The Shift from Personalized to Individualized Therapies, on Thursday, February 13, 2020 at 7:30 AM. Read speaker bios.
Dr. Chester B. Whitley’s Keynote Address: The ‘New’ Lysosomal Disease Network, was on Thursday, February 7, 2019, at 7:30 AM. Read speaker bio.
Dr. Petra Kaufmann delivered her Keynote Address on Wednesday, February 7, 2018 at 8:00 AM as well as Dr. R. Rodney Howell delivered his Keynote Address on Thursday, February 8, 2018 at 7:45 AM. Read speaker bios.
Dr. Elsa Shapiro’s Keynote Address: Understanding and Measuring Neurodegeneration in Childhood Onset Lysosomal Diseases, was on Wednesday, February 15, 2017 at 7:45 AM as well as Dr. Richard Moscicki’s Keynote Address: An FDA Perspective on Rare Disease Drug Development, was on Thursday, February 16, 2017, from 7:45-8:15 AM. Read speaker bios.
Dr. Christopher P. Austin’s Keynote Address: Catalyzing Translational Innovation, was presented at the WORLDSymposium 2016. Read speaker bio.
Dr. Laurie Muldowney’s Keynote Address: The Importance of Natural History Studies and Patient-Focused Data in Drug Development, was at 8:00 AM on Wednesday, February 11, 2015. Read speaker bio.