WORLDSymposium 2019 Keynote Speaker

Chester B. Whitley, PhD, MD Delivered Keynote Address on Wednesday, February 12, 2019. Dr. Whitley is a tenured Professor in the Department of Pediatrics, the Department of Experimental and Clinical Pharmacology, and Director of the Advanced Therapies Program at the University of Minnesota. Read speaker bios.

WORLDSymposium 2019 Patient Advocate Leader (PAL) Award

WORLDSymposium 2022 Patient Advocate Leader (PAL) Award was received by Mark Dant on Wednesday, February 6, 2019. Mark Dant is the Chairman of the Board of the Washington DC-based EveryLife Foundation for Rare Diseases, a science-based advocacy organization dedicated to accelerating biotech innovations for rare disease treatments through science-driven public policy. More details.

WORLDSymposium 2019 Roscoe O. Brady Award

Danilo A. Tagle, PhD, MS received the 2019 Roscoe O. Brady Award for Innovation and Accomplishment. Danilo A. Tagle, PhD, MS, is associate director for special initiatives at NCATS. He also recently served as acting director of the NCATS Office of Grants Management and Scientific Review and currently serves as executive secretary to the NCATS Advisory Council and Cures Acceleration Network Review Board. More details.

WORLDSymposium 2019 Program

Following the presentation of the Roscoe O. Brady Award for Innovation and Accomplishment in lysosomal disease research, presentations in the morning and afternoon sessions discussed innovations in technology and how they can be applied to early diagnosis for lysosomal conditions, progress in gene therapy, and exploitation of differences at the cellular level that may indicate early disease state. View full program.