WORLDSymposium 2019 Program

Following the presentation of the Roscoe O. Brady Award for Innovation and Accomplishment in lysosomal disease research, presentations in the morning and afternoon sessions discussed innovations in technology and how they can be applied to early diagnosis for lysosomal conditions, progress in gene therapy, and exploitation of differences at the cellular level that may indicate early disease state. View full program.

WORLDSymposium 2019 Patient Advocate Leader (PAL) Award

WORLDSymposium 2022 Patient Advocate Leader (PAL) Award was received by Mark Dant on Wednesday, February 6, 2019. Mark Dant is the Chairman of the Board of the Washington DC-based EveryLife Foundation for Rare Diseases, a science-based advocacy organization dedicated to accelerating biotech innovations for rare disease treatments through science-driven public policy. More details.