2021 Satellite Symposia Schedule

Monday, February 08, 2021, 12:00 – 1:00 PM
Interpreting the evidence for Fabry disease: From clinical trials to real-world experience
Supported by Amicus Therapeutics, Inc.
This satellite is open only to registered attendees from outside the United States. International participants only.

Monday, February 08, 2021, 12:00 – 1:00 PM
Hallmarks of Acid Sphingomyelinase Deficiency (ASMD) and Assessment of Disease Progression
Supported by Sanofi Genzyme.

Monday, February 08, 2021, 4:00 – 5:30 PM
Rare Disease Registries: Pioneering Real World Evidence and a Continued Commitment to the Rare Disease Community
Supported by Sanofi Genzyme.

Monday, February 08, 2021, 4:00 – 5:30 PM
The role of Heat Shock Proteins in Lysosomal Storage Diseases
Supported by Orphazyme.
This satellite is open only to registered attendees from inside the United States. US participants only.

Tuesday, February 09, 2021, 12:00 – 1:00 PM
Lysosomal Diseases: Bench to Bedside and Beyond. Understanding immunogenicity, diagnostic testing data, and the potential use of AI
Supported by Sanofi Genzyme.

Tuesday, February 09, 2021, 12:00 – 1:00 PM
Long-term follow-up on MPS IVA – What we have learned
Supported by BioMarin Pharmaceutical Inc.

Tuesday, February 09, 2021, 4:00 – 5:30 PM
Uncovering multiple mechanisms of Fabry disease – implications for management
Supported by Amicus Therapeutics, Inc.

Tuesday, February 09, 2021, 4:00 – 5:30 PM
Pompe Disease Around the World
Supported by Sanofi Genzyme.

Wednesday, February 10, 2021, 12:00 – 1:00 PM
Pompe disease from the inside out: GAA processing, pathogenic cascade and the LOPD patient perspective
Supported by Amicus Therapeutics, Inc.

Wednesday, February 10, 2021, 12:00 – 1:00 PM
Harnessing the Power of Ex-vivo Lentiviral Gene Therapy: A personalized approach
Supported by AVROBIO, Inc.

Wednesday, February 10, 2021, 4:00 – 5:30 PM
Changing Tides in the Management of ASMD: Emerging Treatments and Strategies to Improve Diagnosis
CME Satellite Symposium
Accredited provider: AKH, Inc. (Advancing Knowledge in Healthcare)
Jointly provided by AKH Inc. and Catalyst Medical Education, LLC
Supported by an independent educational grant from Sanofi Genzyme.

Wednesday, February 10, 2021, 4:00 – 5:30 PM
Therapeutic Advances in Metachromatic Leukodystrophy
Supported by Orchard.
This satellite is open only to registered attendees from outside the United States. International participants only.

Thursday, February 11, 2021, 12:00 – 1:00 PM
How has Fabry disease knowledge evolved over the past 20 years? Analysis of recent evidence.
Supported by Sanofi Genzyme.
This satellite is open only to registered attendees from outside the United States. International participants only.

Thursday, February 11, 2021, 12:00 – 1:00 PM
Critical Impact of Inflammation in Lysosomal Diseases: Unlocking Future Treatments and Improving Outcomes
CME/CNE Satellite Symposium
Accredited provider: Postgraduate Institute for Medicine (PIM)
Jointly provided by PIM and Saterdalen & Associates, LLC
Supported by an independent educational grant from Takeda.

Thursday, February 11, 2021, 4:00 – 5:30 PM
Fabry Disease in the Era of COVID-19: Implications for Clinical Practice
Supported by Chiesi USA, Inc.

Thursday, February 11, 2021, 4:00 – 5:30 PM
Unmet need in Gaucher Disease: future possibilities with ex-vivo lentiviral gene therapy
Supported by AVROBIO, Inc.

Friday, February 12, 2021, 12:00 – 1:00 PM
Neurobehavioral and cognitive function in MPS II: a case-led look at effective clinical assessment
Supported by Takeda.

Friday, February 12, 2021, 12:00 – 1:00 PM
Niemann-Pick disease type C: Understanding, evaluating, and treating the disease
Supported by Orphazyme.
This satellite is open only to registered attendees from inside the United States. US participants only.