2023 Satellite Symposia Schedule
Wednesday, February 22, 2023, 6:15 AM – 7:15 AM
Exploring Next-generation Therapies to Mitigate Disease Progression in Pompe Disease
CE Satellite Symposium
Accredited provider: AKH Inc., Advancing Knowledge in Healthcare
Jointly provided by AKH Inc., Advancing Knowledge in Healthcare and Catalyst Medical Education, LLC
Supported by an independent educational grant from Amicus Therapeutics, Inc.
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Wednesday, February 22, 2023, 6:15 AM – 7:15 AM
eDiagnosis: Innovations to Shorten the Rare Disease Diagnostic Journey
Sponsored by Sanofi
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Wednesday, February 22, 2023, 11:45 AM – 12:45 PM
From Assay to Application: Writing the roadmap for metachromatic leukodystrophy newborn screening
Sponsored by Orchard Therapeutics
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Wednesday, February 22, 2023, 11:45 AM – 12:45 PM
First for Fabry Disease: 20-years of Clinical and Real-World Evidence
Sponsored by Sanofi
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Thursday, February 23, 2023, 6:15 AM – 7:15 AM
A treatment option for non-CNS manifestations of acid sphingomyelinase deficiency (ASMD): Patient and HCP perspectives on the transforming ASMD landscape
Sponsored by Sanofi
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Thursday, February 23, 2023, 6:15 AM – 7:15 AM
Manifestations of Gaucher Disease: Rare or Under-recognized?
CE Satellite Symposium
Accredited provider: CME Outfitters, LLC
Supported by an educational grant from Takeda Pharmaceuticals USA, Inc.
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Thursday, February 23, 2023, 11:45 AM – 12:45 PM
The Next Step Forward: Real World Experience in Patients with Late-Onset Pompe Disease
Sponsored by Sanofi
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Thursday, February 23, 2023, 11:45 AM – 12:45 PM
Defining Patient-Focused Outcomes in Fabry Disease
Sponsored by Amicus Therapeutics, Inc.
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Thursday, February 23, 2023, 5:15 PM – 6:15 PM
Understanding Phenotypic Variability in Lysosomal Diseases – Gaining a Foothold in Precision Medicine
Sponsored by Takeda Pharmaceutical Company Limited
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Thursday, February 23, 2023, 5:15 PM – 6:15 PM
Fabry Disease is a Pediatric Disease
Sponsored by Sanofi
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Friday, February 24, 2023, 6:15 AM – 7:15 AM
Following a path to multisystemic efficacy in Fabry disease
Sponsored by Amicus Therapeutics, Inc.
This satellite is open only to registered attendees from outside the United States. International participants only.
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Friday, February 24, 2023, 6:15 AM – 7:15 AM
Uncovering the neurologic impact of enzyme deficiencies along the glycosphingolipid pathway: A case-based discussion
Sponsored by Sanofi
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Friday, February 24, 2023, 11:45 AM – 12:45 PM
Challenges in delivering ERT in lysosomal disorders: Special considerations in LOPD
Sponsored by Amicus Therapeutics, Inc.
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Friday, February 24, 2023, 11:45 AM – 12:45 PM
AAV Gene Therapy as a Potential Treatment Modality for Neuronopathic MPS II
Sponsored by REGENXBIO Inc.
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Friday, February 24, 2023, 5:15 PM – 6:15 PM
One size does not fit all: Monitoring and management of anti-drug antibodies in lysosomal diseases with a focus on Fabry disease
Sponsored by Chiesi Global Rare Diseases
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Friday, February 24, 2023, 5:15 PM – 6:15 PM
MPS IVA in adulthood: Recent findings from the largest global MPS IVA Registry Study
Sponsored by BioMarin Pharmaceutical Inc.
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Saturday, February 25, 2023, 6:15 AM – 7:15 AM
Identifying, Monitoring, and Addressing Risk Factors Impacting Long-term Cardiac, Renal, and Neurological Disease Progression and Clinical Outcomes for Patients with Fabry Disease
CE Satellite Symposium
Accredited provider: Med Learning Group
Supported by an independent educational grant from Sanofi.
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Saturday, February 25, 2023, 11:45 AM – 12:45 PM
The Rare Disease Ecosystem: A multi-stakeholder perspective on collaboration
Sponsored by Sanofi
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Saturday, February 25, 2023, 11:45 AM – 12:45 PM
Pinpointing Alpha-Mannosidosis on the Map: Insights from the diagnostic odyssey of patients
Sponsored by Chiesi Global Rare Diseases
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