Following the opening remarks, presentations in the morning and afternoon sessions will discuss innovations in technology and how they can be applied to early diagnosis for lysosomal conditions, progress in gene therapy, and exploitation of differences at the cellular level that may indicate early disease state. On Tuesday, the noon hour is reserved for a meeting with the WORLDSymposia Council of Patient Advocates (COPA)™ that focuses on patient involvement in research planning and subject recruitment. View full program.
WORLDSymposium 2016 attracted over 25 Exhibitors offering a highly interactive forum for discussion of lysosomal diseases with international researchers and health care practitioners View Exhibitor and Patient Advocate list.
In 2016, over 350 scientific abstracts were presented beginning on Monday, February 29, 2016, and remained open throughout the rest of the conference. View Poster List.
9 Satellite symposia were held from Monday, February 29, 2016 to Thursday, March 3, 2016. Click here for the full schedule.
For the fourth consecutive year, WORLDSymposium began with Emerging Trends in Lysosomal Biology & Lysosomal Diseases: State-of-the-art for Experts on Monday, February 29, 2016. See agenda and faculty.
Three postdoctoral Lysosomal Disease Network Fellows were selected by the LDN Steering Committee. More Details.
WORLDSymposium was pleased to announce the 8 recipients of the 2016 Young Investigator Awards. Click to view award recipients.
The WORLDSymposium 2016 New Treatment Award was presented to sebelipase alfa (Kanum™). More details.
WORLDSymposium 2016 Award for Innovation and Accomplishment was presented to Dr. Emil Kakkis. Dr. Kakkis is President and Chief Executive Officer of Ultragenyx Pharmaceutical where he leads a drug development team working on multiple rare and ultra‐rare disease treatments. More details.
WORLDSymposium 2016 Patient Advocate Leader (PAL) Award was received by Barbara Wedehase. Barbara Wedehase has a Masters in Social Work from Washington University in St. Louis, Missouri and is a Board Certified Genetic Counselor.More details.
Christopher P. Austin, MD, Delivered Keynote at WORLDSymposium 2016. Dr. Austin is director of the National Center for Advancing Translational Sciences (NCATS) at the National Institutes of Health (NIH). Read speaker bios.