WORLDSymposium 2022 Robert J. Gorlin Symposium

The inaugural Robert J. Gorlin Symposium discussed the urgent need to develop and implement precise metrics for measuring cognitive change in children with lysosomal diseases. Precision Metrics for Cognition brought together leading experts to provide an explanation and rationale for using growth scale values (GSVs) to measure developmental longitudinal cognitive change in children with early onset and severe lysosomal diseases. More details.

WORLDSymposium 2022 Program

After the presentation of the Innovation Award, the formal scientific sessions of WORLDSymposium 2022 officially began with presentations on laboratory research for lysosomal disease. Presentations during the Basic Science sessions are designed to improve our understanding or prediction of the phenomena involved in lysosomal pathology at a molecular, cellular, and animal model level in order to forwardly think about diagnosis and treatment of lysosomal conditions. View full program.

WORLDSymposium 2022 Exhibitors

WORLDSymposium 2022 attracted over 40 Exhibitors offering a highly interactive forum for discussion of lysosomal diseases with international researchers and health care practitioners. More details.

WORLDSymposium 2022 Patient Advocate Leader (PAL) Award

WORLDSymposium 2022 Patient Advocate Leader (PAL) Award was received by Sue Kahn on Tuesday, February 8, 2022. For 14 years, Sue has served as the Executive Director of the National Tay-Sachs & Allied Diseases Association (NTSAD) that supports families affected by Tay-Sachs, Canavan, GM1, and Sandhoff. More details.

WORLDSymposium 2022 Keynote Speaker

Tippi Mackenzie, MD was the Keynote Speaker on Wednesday, February 9, 2022. Tippi MacKenzie is a Professor of Surgery at the University of California, San Francisco and the Director of the Eli and Edythe Broad Institute for Regeneration Medicine. Read speaker bio.

WORLDSymposium 2022 Roscoe O. Brady Award

WORLDSymposium 2022 Roscoe O. Brady Award was received by Stuart A. Kornfeld, MD for Innovation and Accomplishment on Monday, February 7, 2022 Stuart A. Kornfeld, MD, is the David C. and Betty Farrell Professor of Medicine at Washington University in St. Louis. More details.